Tim Miller, Ph.D., President & CEO
PlasmaTech Biopharmaceuticals/Abeona Therapeutics is focused on developing and delivering gene therapy and plasma-based products for severe and life-threatening rare diseases. PlasmaTech’s lead program is a gene therapy for Sanfilippo syndrome (MPS IIIA and IIIB) in collaboration with patient advocate groups, researchers and clinicians. In addition, the company is pursuing two additional proprietary platforms, Salt Diafiltration (SDF™) Process and Polymer Hydrogel Technology (PHT™), and is active in the development and commercialization of human plasma-derived therapeutics, including its proprietary
NantKwest – Immunotherapy company focused on harnessing the power of the innate immune system by using the natural killer cell to treat cancer, infectious diseases and inflammatory diseases. Natural killer, or NK, cells are the body’s first line of defense due to their innate ability to rapidly seek and destroy abnormal cells, such as cancer or virally-infected cells, without prior exposure or activation by other support molecules required to activate adaptive immune cells such as T-cells.… Read more
The immune system is the body’s natural defence system. It is a collection of organs, cells and special molecules that helps protect you from infections, cancer and other diseases. When a different (foreign) organism enters into the body, for example a bacteria, the immune system recognises it and then attacks it, preventing it from causing harm. This process is called an immune response. Since cancer cells are very different from normal cells in the body, the immune system attacks them when it is able to recognise them. However, cancer cells … Read more
Researchers are developing ways to use CRISPR to treat genetic conditions like sickle-cell anemia and cystic fibrosis, and are also experimenting with genetic changes that could eliminate viruses like HIV. Even though viruses aren’t genetic diseases, certain gene edits have been shown to prevent the virus from spreading to new cells and to “destroy inactive HIV residing in the human genome by altering critical viral genes,” according to a look at genome surgery in MIT Tech Review. Experts even think these types of changes could eventually help treat complex conditions … Read more
All you need to know about Cellectis :
4 branchs :
-Cellectis Plants Science (CPS)
Corporate presentation : urlz.fr/1AWL
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http://www.nature.com/srep/2015/150130/srep08150/full/srep08150.html… Read more
Studying the muscle stem cells in boys suffering fromDuchenne muscular dystrophy, Stanford scientist Helen Blau found that their telomeres–the protective caps at the end of chromosomes–were unusually short. Now, in a new study, Blau and a small group of colleagues say that they have developed a method to use modified messenger RNA to lengthen telomeres, opening a pathway to countering the effects of aging in cells–a process that might apply to a range of diseases from DMD to diabetes and heart disease.
Telomeres naturally shorten every time a … Read more
The FDA is evaluating proposals for new indications for at least 17 oncology medicines, according to Friends of Cancer Research. The list of therapies includes novel agents and existing drugs whose uses could be expanded if the agency approves the applications.
The breakthrough therapy program is designed to streamline drug development for therapies to treat serious and life-threatening illnesses. The FDA grants the status based on whether a therapy would provide a substantial improvement over existing options based on preliminary clinical evidence.
The Friends advocacy group helped promote the concept … Read more