Monthly Archives: August 2015
CRISPR – EMBRYO EDITING
https://flipboard.com/@naturenewsteam/embryo-editing%3A-the-ethics-of-crispr-27j1164kz
A new genetic engineering technology called CRISPR/Cas9 has opened the door to unprecedented tinkering with the human genome. Nature takes a look at the scientific possibilities and the ethical dilemmas they raise.… Read more
Gene Therapy and regenerative medicine companies.
ABEONA THERAPEUTICS
Tim Miller, Ph.D., President & CEO
Dallas, TX
(NASDAQ: ABEO)
PlasmaTech Biopharmaceuticals/Abeona Therapeutics is focused on developing and delivering gene therapy and plasma-based products for severe and life-threatening rare diseases. PlasmaTech’s lead program is a gene therapy for Sanfilippo syndrome (MPS IIIA and IIIB) in collaboration with patient advocate groups, researchers and clinicians. In addition, the company is pursuing two additional proprietary platforms, Salt Diafiltration (SDF™) Process and Polymer Hydrogel Technology (PHT™), and is active in the development and commercialization of human plasma-derived therapeutics, including its proprietary
Sorrento Therapeutics
All About Oncology
Global Blood Therapeutics – respiratory distress syndrome
Global Blood Therapeutics initially focusing on indications with significant unmet need, including idiopathic pulmonary fibrosis (IPF) and acute respiratory distress syndrome (ARDS), in which hypoxia is believed to play a key role in disease pathogenesis and adverse patient outcomes. These are conditions in which the lungs cannot supply adequate oxygen to the blood. While supplemental oxygen therapy is a well-established lifesaving treatment in acute and chronic hypoxemic conditions, it is associated with a number of risks, including injury or infection as a result of intubation. This highlights a significant unmet … Read more
Aimmune Therapeutics – Treatment of peanut allergy
Aimmune Therapeutics – Treatment of peanut allergy… Read more
Zynerba Pharmaceuticals – Synthetic Cannabinoid
Synthetic cannabinoid therapeutics for transdermal delivery system.
First and Only Synthetic CBD Formulated as a Permeation-Enhanced Gel Being Studied in Refractory Epilepsy, Fragile X Syndrome and Osteoarthritis… Read more
Lead products from top RNAi technology companies.
RNAi Lead products from top companies.
- ALN-TTR02 (patisiran)
- Vigil immunotherapy
- ALN-TTRsc (revusiran)
- ARC-520
- Atu027
- PF-655
- QPI-1002
- RXI-109
- siG12D-LODER
- SPC3649 (miravirsen)
- SYL04001
RNAi Technology companies
Acuity Pharmaceuticals (now OPKO Health)
Advirna
Aegera Therapeutics
Agilent Technologies
Alcon (subsidiary of Novartis)
Alexion
Allele Biotechnology
Allergan
Almirall
Alnylam
Altogen Labs
AmpliPhi Biosciences
Antisense Therapeutics
AptaBio
Aptose Biosciences
Arcturus Therapeutics
ArmaGen Technologies
Arrowhead Research
Ascletis Pharmaceuticals
AstraZeneca
Atugen AG (acquired by Silence Therapeutics)
Avecia OligoMedicines
Bayer
Benitec Biopharma
Biocon
Biogen Idec
Biomatik Corporation
Biomics Biotechnologies
Biomics Biotechnology
Bionexus
BioNTech
BioSpring
BioSpring GmbH
Bio-Synthesis
Blueberry Therapeutics
Bristol-Myers Squibb
Calando Pharmaceuticals (subsidiary of Arrowhead)
Celsion
CRISPR Therapeutics
Cubist Pharmaceuticals (acquired by Merck)
CureVac
Dainippon Sumitomo
Dendreon
Dharmacon RNAi Technologies (part … Read more