- AAV – adeno-associated virus
- Ad-Endo – adenovirus expressing endostatin
- ALL – acute lymphoid leukemia
- AML – acute myeloid leukemia
- ART – antiretroviral therapy
- ATI – analytic treatment interruption
- AZT – zidovudine
- cART – combination antiretroviral therapy
- CD – cytosine deaminase
- CGD – chronic granulomatous disease
- CHC – chronic hepatitis C
- CNS – central nervous system
- CSF – cerebrospinal fluid
- CT – computed tomography
- DLTs – dose-limiting toxicities
- EP – electroporation
- FDA – Food and Drug Administration, HHS
- 5FC – flucytosine
- 5FU – 5-fluorouracil
- GAN – giant axonal neuropathy
- GCC – guanylyl cyclase C
- G-CSF – granulocyte colony stimulating factor
- GFP – green fluorescent protein
- GI – gastrointestinal
- GLP – “Good Laboratory Practices”
- GTSAB – Gene Transfer Safety Assessment Board
- GVHD g – raft-versus-host disease
- HCV – hepatitis C virus
- HHS – U.S. Department Health and Human Services
- hGCC – human guanylyl cyclase C
- HGG – high-grade glioma
- HLA – human leukocyte antigen
- HPV – human papillomavirus
- HSCs – hematopoietic stem cells
- HSCT – hematopoietic stem cell transplantation
- HSV – herpes simplex virus
- IC – intracranial
- IC-IT – intracranial-intratumoral
- ICV – intracerebral-ventricular
- IM – intramuscular
- IMRT – intensity-modulated radiation therapy
- IND – Investigational New Drug
- IRB – institutional review board
- IV – intravenous
- MDS – myelodysplastic syndrome
- miRNA – micro RNA
- MLV – murine leukemia virus
- MRI – magnetic resonance imaging
- NAA – N-acetylaspartate
- NCCN – National Comprehensive Cancer Network
- NIAID – National Institute of Allergy and Infectious Diseases, NIHNIH National Institutes of Health
- NINDS – National Institute of Neurological Disorders and Stroke, NIH
- NK – natural killer
- NSG – NOD SCID gamma
- OBA – Office of Biotechnology Activities, NIH
- OD – Office of the Director, NIH
- PBMCs – peripheral blood mononuclear cells
- PBSC – peripheral blood stem cell
- RAC – Recombinant DNA Advisory Committee
- RT-PCR – reverse transcription polymerase chain reaction
- SAE – serious adverse event
- shRNAs – short hairpin RNAs
- SIV – simian immunodeficiency virus
- UNC – University of North Carolina at Chapel Hill
- WAS – Wiskott-Aldrich Syndrome
- WASp – Wiskott-Aldrich Syndrome protein
- XCGD – X-linked chronic granulomatous disease